Therapeutic Area Experience

Rare/orphan disease

Neurology (myasthenia gravis, chronic inflammatory demyelinating polyneuropathy, mitochondrial myopathies, necrotizing autoimmune myopathy, Lambert-Eaton Syndrome)

Rheumatology (rheumatoid arthritis, Sjogren’s disease, systemic sclerosis, osteoarthritis)

Cardiovascular (catecholaminergic polymorphic ventricular tachycardia, pulmonary arterial hypertension, heart failure [HFpEF and HFrEF], transthyretin amyloidosis with cardiomyopathy, Barth’s Syndrome)

Nephrology (acute kidney injury, chronic kidney disease, lupus nephritis, IGA nephropathy)

Endocrinology (Graves disease)

Gastrointestinal (opioid-induced constipation, post-operative ileus)

Dermatology (dermatomyositis, cutaneous lupus erythematosus, pemphigus vulgaris)

Ophthalmology (Leber’s Hereditary Optic Neuropathy, thyroid eye disease, age related macular degeneration, age-related macular degeneration)

Pulmonology (cystic fibrosis)

Immunology (antibody mediated rejection, AAV vector desensitization)

Hematology (Gaucher Disease Type 1, warm autoimmune hemolytic anemia, immune thrombocytopenia)

Reproductive health (preeclampsia)

Anti-infectives (Gram-positive and Gram-negative infections)

Pain management (acute nociceptive pain, chronic/persistent postoperative pain)